About Cerliponase Alfa
Class: | Enzyme replacement therapy
Use: | Treatment of neuronal ceroid lipofuscinosis type 2 (CLN2) in pediatric patients aged 3 years and older
Adult dose: | Not established; primarily indicated for pediatric use
Pediatric dose: | 300 mg (10 ml) administered intraventricularly every 14 days
Side effects: | Seizures, headache, fever, vomiting, and irritability
Contraindications: | Hypersensitivity to cerliponase alfa or any component of the formulation
Storage: | Store in the refrig
Drug Class
Enzyme replacement therapy
Uses & Indications
Treatment of neuronal ceroid lipofuscinosis type 2 (CLN2) in pediatric patients aged 3 years and older
Storage Requirements
Store in the refrigerator at 2°C to 8°C (36°F to 46°F); do not freeze; protect from light
Manufacturer & Packaging
Manufacturer: BioMarin Pharmaceuticals, U.S.A
Package Size
Vial x 2
Price & Supplier
Price in UAE: AED 112413.00
Dosage Information
Adult Dose
Not established; primarily indicated for pediatric use
Pediatric Dose
300 mg (10 ml) administered intraventricularly every 14 days
Side Effects
Seizures, headache, fever, vomiting, and irritability
Contraindications & Precautions
Hypersensitivity to cerliponase alfa or any component of the formulation
Important Warnings
Risk of serious adverse reactions including hypersensitivity reactions; monitor for seizures and other neurological symptoms during treatment
Medical Disclaimer
This information is for educational purposes only and should not replace professional medical advice.
Always consult with a licensed healthcare provider or pharmacist in the UAE before taking any medication.
The information presented here is specific to medicines available in UAE pharmacies and is regularly updated
to ensure accuracy for patients and healthcare professionals in the United Arab Emirates.