Complete List of Antisense oligonucleotide Medicines
Brand: AMONDYS 45 |
Strength: 50 mg/ml |
Form: Solution For Dilution For Intravenous Infusion
Class: | Antisense oligonucleotide
Use: | Casimersen (AMONDYS 45) is used for the treatment of Duchenne muscular dystrophy (DMD) in patients who have a confirmed mutation of the DMD gene that is amena...
Brand: EXONDYS 51 |
Strength: 50 mg/ml |
Form: Solution For Injection
Class: | Antisense oligonucleotide
Use: | Eteplirsen is indicated for the treatment of Duchenne muscular dystrophy (DMD) in patients who have a confirmed mutation of the DMD gene that is amenable to e...
Brand: WAINUA |
Strength: 45 mg/0.8ml |
Form: Solution For Injection
Class: | Antisense oligonucleotide
Use: | Treatment of transthyretin amyloidosis (ATTR)
Adult dose: | 45 mg administered subcutaneously once weekly
Pediatric dose: | Safety and efficacy not esta...
Brand: QFITLIA |
Strength: 20 mg |
Form: Solution For Injection
Class: | Antisense oligonucleotide therapy
Use: | Treatment of hemophilia A or B in patients with inhibitors to factor VIII or IX
Adult dose: | 50 mg subcutaneously once every 4 weeks
Pediatric ...
Brand: QFITLIA |
Strength: 50 mg |
Form: Solution For Injection
Class: | Antisense oligonucleotide therapy
Use: | Treatment of hemophilia A or B in patients with inhibitors to factor VIII or IX
Adult dose: | 50 mg subcutaneously once monthly
Pediatric dose: ...
Brand: VYONDYS 53 |
Strength: 50 mg/ml |
Form: Solution For Dilution For Intravenous Infusion
Class: | Antisense oligonucleotide
Use: | Golodirsen is indicated for the treatment of Duchenne muscular dystrophy (DMD) in patients who have a confirmed mutation of the DMD gene that is amenable to e...
Brand: OGSIVEO |
Strength: 50 mg |
Form: Film Coated Tablets
Class: | Antisense oligonucleotide therapy
Use: | Treatment of patients with amyotrophic lateral sclerosis (ALS) associated with a specific genetic mutation (SOD1-ALS)
Adult dose: | 50 mg administ...
Brand: SPINRAZA |
Strength: 12 mg/5ml |
Form: Intrathecal Injection
Class: | Antisense oligonucleotide
Use: | Treatment of spinal muscular atrophy (SMA) in patients with 5q chromosome deletion
Adult dose: | Not established; primarily used in pediatric patients
P...
Brand: SPINRAZA |
Strength: 12 mg/5ml |
Form: Intrathecal Injection
Class: | Antisense oligonucleotide
Use: | Treatment of spinal muscular atrophy (SMA) in patients with 5q SMA, including infants, children, and adults
Adult dose: | Initial dose of 12 mg intratheca...
Brand: SPINRAZA |
Strength: 2 mg/5ml |
Form: Intrathecal Injection
Class: | Antisense oligonucleotide
Use: | Treatment of spinal muscular atrophy (SMA) in pediatric and adult patients
Adult dose: | 12 mg (3 mL) administered intrathecally once every 4 months after...
Brand: QALSODY |
Strength: 100 mg/1 vial |
Form: Solution For Injection
Class: | Antisense oligonucleotide
Use: | Treatment of amyotrophic lateral sclerosis (ALS) associated with superoxide dismutase 1 (SOD1) mutations
Adult dose: | 100 mg administered as a subcutaneo...